The tiny zebrafish is helping researchers rapidly determine whether a newborn's genetic mutation is likely to cause spinal ...

The mother of a four-year-old boy with a rare muscle disease says screening newborn babies for the condition could "save ...

A couple whose son died from a rare genetic condition are encouraging others to take part in screening which they say could ...

Is your backside trying to tell you something? New research suggests that the shape of the GM — not just the size — could be ...

On January 4, former Little Mix singer Jesy Nelson took to Instagram to reveal that her twins have been diagnosed with spinal muscular atrophy (SMA) type 1, which is a genetic neuromuscular condition ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

What is SMA? The rare genetic condition that Jesy Nelson’s twins have - Former Little Mix star revealed her twin daughters had been diagnosed with Spinal Muscular Atrophy (SMA) Type 1 ...

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Topline results from a phase 3 clinical trial showed an ...

Spinal muscular atrophy explained after Jesy Nelson reveals her twins’ diagnosis - The singer shared an emotional update about her twins’ health on Sunday and that ‘time is of the essence with this di ...

The 34-year-old singer recently shared the devastating news that her children have Spinal Muscular Atrophy Type 1, which ...