Two of Opus's seven gene therapy assets are in clinical trials, with additional programs expected to enter the clinic.

More people are turning to genetic counseling to understand their DNA and assess their risk for certain diseases. As part of ...

Emily Kramer-Golinkoff can’t get enough oxygen with each breath. Advanced cystic fibrosis makes even simple things like walking or showering arduous and exhausting. She has the most common fatal ...

Next-generation cancer tests are being developed here in Houston, and the HBJ pulled back the curtain on how one partnership ...

Mutations in the tumor suppressor TP53 are a common cause of cancer, making the altered protein an attractive target for ...

Researchers from Radboud university medical center and University of Basel have discovered new genetic causes of inherited ...

Meet the luckiest people on Earth — individuals carrying a rare genetic mutation that prevents wrinkles from forming even as they age well into their 80s. These genetic lottery winners have provided ...

This photo provided by Emilys Entourage in April 2025 shows Emily Kramer-Golinkoff, who has cystic fibrosis caused by a rare genetic mutation, during a trip to Maine. (Emilys Entourage via AP) ...